Healthy Living

New Muscular Dystrophy Drug Granted FDA Orphan Designation in US

What can patients and their families do?

BB-301 is certainly very firmly placed on the horizon of treatment options for patients with OPMD, but the reality is that it’s not available just yet.  So what should you do while you wait?  Well, first things first, find out the treatment options that are available now and with the support of a medical team, try to implement them. Join support groups and research resources to learn better ways to live with the disease. But, most importantly, stay positive and hold onto hope that new treatment options will become available soon.